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Disease Reportsparoxysmal hemoglobinuria
MeSH D006457 - paroxysmal hemoglobinuria
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D009190:Myelodysplastic syndromes
$
Success rate
D000743:Hemolytic anemia
D006457: 
Paroxysmal hemoglobinuria
$
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
Alexion PharmaceuticalsEculizumab Soliris  2007-03-16 $4,068.9 M Q2/20-Q1/21 
Ravulizumab Ultomiris  2019-07-02 $1,200.8 M Q2/20-Q1/21 
AmgenEculizumab Bekemv  2023-04-19   
Orphan MedicalPegcetacoplan Aspaveli  2021-12-13   
Clinical Trials
Historical Success Rate
Phase 1
40%
2/5
Phase 2
23%
9/39
Phase 3
64%
9/14
Approved: 5Overall Success rate: 6%
All Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Company name
Phase 1
Phase 2
Phase 3
Phase 4
Drug Name
Alexion Pharmaceuticals
Amgen
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